Our new Research Fund

We recently launched our new Research Fund, introduced to help find cures for children with life-threatening and life-limiting diseases. Here's what you need to know.

As part of the Discovery Appeal, the Research Fund will contribute to the overall £50 million target we've pledged to raise to help find faster diagnoses, life-changing cures and kinder treatments through research. 

Why we believe 

30% of children with rare diseases lose their life before their fifth birthday. We believe in the power of research to prevent this tragic loss of young lives. 

GOSH Charity is the UK's largest dedicated funder of child health research. Our funding has helped drive pioneering breakthroughs, such as the first use of gene therapy to successfully give children born without an immune system their lives back.

Every single day, over 900 life-saving research projects are active across GOSH and its dedicated research Institute. We’re asking for a donation of £5 a month to help find more breakthroughs that will change young lives.

Donate now

Meet Jake

As part of the launch, we met with a group of patients currently undergoing pioneering treatment at GOSH. 

One of those patients is Jake, who was diagnosed with Duchenne Muscular Dystrophy (DMD) – a progressive condition where muscles waste away – when he was three years old. 


Jake's parents made the decision to enrol Jake in a research trial at GOSH, commenting they would travel to the ends of the Earth for anything that could help him. 

Jake’s family learned about Professor Muntoni’s clinical trial and met with him to discuss the study in detail. 

“Right from our first meeting, Professor Muntoni was great,” says Jake’s dad Carl. “He showed us a video and explained what the trial involved and what sort of expectation they had of how it would work.” 

Jake’s trial is coming to an end, at which point Professor Muntoni and his team will analyse the results, but the family will continue receiving this treatment and have high hopes for the future.

Learn more about our Research Fund