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Kai's story: One of the first patients to be treated at the Zayed Centre for Research

Our brand new medical facility, the Zayed Centre for Research into Rare Disease in Children, brings together pioneering research and clinical care under one roof to drive forward new treatments and cures for seriously ill children, both across the UK and internationally. One of the first patients to be treated at the Centre is Kai, aged 10. 

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Meet Nina

One of the main areas of research within the Zayed Centre for Research will be to develop new gene therapy approaches to offer transformative and curative therapies for a wide range of genetic diseases. Gene therapy involves inserting a working copy of a faulty gene into a patient's own cells so that they start to work correctly. Since 2001, more than 70 children have been treated with gene therapy for immune system disorders at GOSH including Nina, aged 7. Her dad Graeme shares their story: